New FDA Drug for Rare Disease: A First-Time Approval

FDA Approves Leucovorin for Cerebral Folate Deficiency, Following Autism Research Discussion In a landmark decision, the Food and Drug Administration (FDA) has granted approval for the use of leucovorin in treating cerebral folate deficiency, a rare genetic disorder. This approval arrives several months after FDA Commissioner Dr. Marty Makary publicly highlighted the potential of this … Read more