Zolgensma Repeat Dose: SMA Treatment Outcomes & Safety
New Hope for Spinal Muscular Atrophy: Phase 3 Trial Shows Promise of Intrathecal Gene Therapy In a significant advancement for the treatment of spinal muscular atrophy (SMA), results from the Phase 3 STRENGTH study indicate that intrathecal onasemnogene abeparvovec demonstrates a favorable safety profile and offers a potential new therapeutic avenue for individuals affected by … Read more